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ARN Acetylcholinesterase deficiency Therapy Dilated cardiomyopathy Heart Cell culture model Skeletal muscle Muscular dystrophy Astrocytes DMPK Gene Therapy Humans RNA splicing RNA biology CTG repeat contractions Intermediate filament Quantitative microdialysis Myostatin Maximal force Glucocorticoid-receptor CRISPR/Cas9 Myotonic Dystrophy Type 1 AAV Trinucleotide Repeat Expansion In vivo Expression Muscle ACETYLCHOLINESTERASE Thérapie génique GABA Motoneuron GSK3␤ Desmin CRISPRi Cell model CTG repeats Glucocorticoids Brain dysfunction Long read sequencing Myotonic dystrophy mouse models Cardiac muscle Oligodendrocyte Gene therapy Dystrophie Myotonique Genotype phenotype correlation CONGENITAL MYATHENIC SYNDROME Glial cells Aging CTG repeat instability Cytoskeleton Neuron Mouse model PacBio KNOCKOUT MICE Myelin Mouse models Heart failure Diaphragm Mice Dystrophie myotonique Transgenic mouse model Brain Dynamin 2 Knockout DMSXL mice Antisense oligonucleotide Glutamate PCR Myotonic Dystrophy type 1 Antisense oligonucleotides Animals Exercice Transcriptomics Central nervous system Gene editing Myotonic dystrophy type 1 Myotonic Dystrophy Acetylcholinesterase knockout mouse BIOLOGIE MOLECULAIRE Oligodendrocytes RNA interference DM1 MBNL Transgenic mouse Autophagy Astrocyte Duchenne muscular dystrophy Myotonic dystrophy Fibrosis Dystrophin Exercise Endurance training Trinucleotide repeat expansion Alternative splicing Centronuclear myopathy Acute coronary syndrome Cell penetrating peptide Male CMS Hypoxia